Harvard Catalyst Profiles
Contact, publication, and social network information about Harvard faculty and fellows.
Home
About
Overview
Open Source Software
Help
History (1)
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
See All Pages
Find People
Find Everything
Login
to
edit your profile
(add a photo, education, awards, etc.), search
student opportunities
, and
create reports
.
Edit My Profile
My Person List (
0
)
Opportunity Search
Return to Top
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice.
Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice. Mol Ther. 2015 May; 23(5):835-844.
View in:
PubMed
subject areas
Animals
Antigens, CD
Antigens, Differentiation, Myelomonocytic
Disease Models, Animal
Enzyme Activation
Gaucher Disease
Gene Expression
Gene Order
Gene Transfer Techniques
Genetic Vectors
Glucosylceramidase
Humans
Lentivirus
Macrophages
Mice
Mice, Knockout
Organ Specificity
Phenotype
Promoter Regions, Genetic
Transduction, Genetic
Transgenes
Virus Integration
authors with profiles
Axel Schambach, Ph.D.